News + Seminars | N=1 Collaborative

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Personalized medicine for rare neurogenetic disorders: can we make it happen?

A framework for N-of-1 trials of individualized gene-targeted therapies for genetic diseases

Olivia Kim-McManus, Joseph G. Gleeson, Laurence Mignon, Amena Smith Fine, Winston Yan, Nicole Nolen, Scott Demarest, Elizabeth...

Phage Therapy for Multidrug-Resistant Bacterial Infections: Past and Future

SNP-selective siRNA for the treatment of Fibrodysplasia Ossificans Progressiva

The state-of-the-art of N-of-1 therapies and the IRDiRC N-of-1 development roadmap

Treating the Nano-Rare: Redefining Clinical Management, One Patient at a Time

Workshops & Presentations

N1C VARIANT Workshop

Illustrated Examples

Positive and negative controls for ssASOs and Gapmers that can be used for in vitro tox studies

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