Seminar SeriesFast Track to Final Drug Product: Understanding Costs, Challenges, and Timelines in Personalized Medicine Manufacturing
PublicationsPractical Recommendations for the Selection of Patients for Individualized Splice-Switching ASO-Based Treatments
Seminar SeriesPRAX-222 Therapy for a Child: Prenatal Onset SCN2A Developmental and Epileptic Encephalopathy in a Named Patient Setting
Illustrated ExamplesN1C Preclinical Workgroup: Valuable Tools for the Preclinical Stage of Developing Potential Therapeutics Click below for download
Seminar Series"Control of starting material quality for oligonucleotide therapeutics" and "To Synthesis and Beyond…Production of oligos for ‘N-of-1’ therapies"
