Our Work
Our Work
Our Mission
N1C is the professional home for interventional genetics. We enable the ecosystem by convening and connecting practitioners and developers to exchange knowledge, collaborate, set the tone for responsible innovation, and guide the standards that advance the field.
Our collective work takes shape across three areas — knowledge, resources, and data.
Sharing Knowledge
Equipping the ecosystem with the insights, education, and guidance needed to scale individualized medicine
Seminars
Ongoing virtual sessions bring together experts across research, clinical care, and patient advocacy. Topics span technical insights, case studies, lessons learned, and systems-level challenges of the individualized medicine ecosystem.
Podcast
Fireside Chats in Individualized Medicine features conversations with leaders and emerging voices across the individualized medicine ecosystem. Episodes explore technical strategy and evolving approaches to individualized therapies. The podcast is available to stream through Spotify, Apple Podcasts, Amazon Music, and Connections.
Workgroups
N1C workgroups bring together multidisciplinary experts to address specific challenges in individualized therapy development. Eight cross-sector workgroups develop practical tools and standards including consensus guidelines for therapeutic actionability, publications, illustrated examples, articles, workshops and presentations.
Sharing Knowledge
Equipping the ecosystem with the insights, education, and guidance needed to scale individualized medicine
Seminars
Ongoing virtual sessions bring together experts across research, clinical care, and patient advocacy. Topics span technical insights, case studies, lessons learned, and systems-level challenges of the individualized medicine ecosystem.
Podcast
Fireside Chats in Individualized Medicine features conversations with leaders and emerging voices across the individualized medicine ecosystem. Episodes explore technical strategy and evolving approaches to individualized therapies. The podcast is available to stream through Spotify, Apple Podcasts, Amazon Music, and Connections.
Workgroups
N1C workgroups bring together multidisciplinary experts to address specific challenges in individualized therapy development. Eight cross-sector workgroups develop practical tools and standards including consensus guidelines for therapeutic actionability, publications, illustrated examples, articles, workshops and presentations.
Sharing Resources
Enabling faster and more equitable development by connecting teams to the tools, materials, and guidance they need
Donated Resource Center
The Donated Resource Center mobilizes in-kind goods and services to support individualized therapy efforts for patients with urgent needs. By coordinating contributions across the ecosystem, the center helps reduce barriers and accelerate progress for research and clinical teams.
Connections
Connections is N1C’s community platform for open discussion, resource sharing, collaboration, and problem solving.
N1C VARIANT
N1C VARIANT (Variant Assessments Towards Eligibility for Antisense Oligonucleotide Treatment) provides tools and guidance to support eligibility assessment for individualized therapies. VARIANT represents a step toward more standardized, transparent approaches to evaluating treatment eligibility.
Sharing Resources
Enabling faster and more equitable development by connecting teams to the tools, materials, and guidance they need
Donated Resource Center
The Donated Resource Center mobilizes in-kind goods and services to support individualized therapy efforts for patients with urgent needs. By coordinating contributions across the ecosystem, the center helps reduce barriers and accelerate progress for research and clinical teams.
Connections
Connections is N1C’s community platform for open discussion, resource sharing, collaboration, and problem solving.
N1C VARIANT
N1C VARIANT (Variant Assessments Towards Eligibility for Antisense Oligonucleotide Treatment) provides tools and guidance to support eligibility assessment for individualized therapies. VARIANT represents a step toward more standardized, transparent approaches to evaluating treatment eligibility.
Sharing Data
Advancing discovery and development through collaborative data infrastructure
Gene Registry
The Gene Registry is a global catalog of individualized therapy programs, marketed gene therapies, and assessed variants — designed to increase visibility and coordination across efforts. The registry helps connect researchers, clinicians, and patient communities working on similar challenges.
Preclinical Database
Coming Soon
Clinical Database
Coming Soon
Sharing Data
Advancing discovery and development through collaborative data infrastructure
Gene Registry
The Gene Registry is a global catalog of individualized therapy programs, marketed gene therapies, and assessed variants — designed to increase visibility and coordination across efforts. The registry helps connect researchers, clinicians, and patient communities working on similar challenges.
Preclinical Database
Coming Soon
Clinical Database
Coming Soon